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PREMIUM RESEARCH REPORT
Outlook: Bullish

Alnylam Pharmaceuticals (ALNY) In-Depth Stock Report

The leading RNA interference company, priced on its transthyretin franchise, pipeline breadth, and path to sustained profitability.

Published 2026-09-21·Updated 2026-09-21·HealthcareBiotechnology

Investment Summary

Every headline number this report produces, collected in one place before the analysis that derives them. All figures are computed live at page load, so this block reflects the market as of the moment you opened the page.

Current Price
$244.32
Outlook
Bullish
(directional lean, see note below)
Valuation Verdict
Above fair value
(vs. our relevance-weighted range)
Fair Value Range
$35 – $173
12-Month Price Target
$292.43
(model + consensus blend)
Expected Return to Target
+19.7%
AI Score
53 / 100
(vs. our covered universe)
Risk Rating
Moderate
(risk factor 42/100, lower is riskier)
Target Confidence
High
Horizon
12 months
(target and scenarios)
Why we hold this view
  • Cardiomyopathy uptake exceeds expectations.
  • Profitability expands quickly.
  • Pipeline programs succeed.
  • The platform yields additional approvals.
"Outlook" is a plain-language summary of our expected return to the 12-month price target (Bullish ≥ 8% upside, Bearish ≤ 8% downside, Neutral in between; falls back to the fair-value comparison when no target is available) — it is a restatement of the figures above, not a new signal, and like them is not a buy or sell recommendation. "Valuation Verdict" compares the live price to our relevance-weighted fair-value range and is a statement about our own model's output, not a buy or sell recommendation — see the Investor Decision Framework near the end of this report. The risk rating is derived from AI Score risk factor rather than assigned by hand. Expected return measures the gap to the 12-month blended target only; it is not a forecast of total return and excludes any dividend.
ALNY in 60 Seconds
  • Alnylam is the leading RNA interference company.
  • Transthyretin disease drives growth.
  • Competition and pipeline risk are the main risks.
  • Product revenue and profitability are the key numbers.
What's inside this report
  • Alnylam pioneered RNA interference, a method that silences disease-causing genes, and has several approved medicines.
  • Its largest opportunity is treating transthyretin amyloidosis, a disease affecting the heart and nerves.
  • The company moved from long losses toward profitability as product revenue grew.
  • A pipeline includes programs in cardiometabolic disease and neurological conditions.
  • The equity debate is the pace of transthyretin cardiomyopathy uptake versus competition from other approaches.

Executive Summary

Alnylam has validated its platform with multiple approved products and licensing arrangements with major partners.

The transthyretin cardiomyopathy market is large, with newer treatment options expanding diagnosis and awareness.

RNAi drugs can be dosed infrequently, an attractive feature for chronic diseases, and the company uses a consistent delivery approach across programs.

Growth has driven rapid revenue expansion, and the company has been working toward sustained profit and cash generation.

The realistic thesis: a platform biotech with real commercial traction and high expectations, where sales growth in transthyretin disease and pipeline delivery determine outcomes.

Industry & Market Backdrop

The broader competitive and macro environment ALNY operates in — context a pure valuation table can't convey on its own.

Diagnosis of transthyretin cardiomyopathy is rising as awareness improves.

Competition includes stabilizers and other gene-silencing approaches.

Investors have favored biotechs with clear commercial traction and manageable cash burn.

Payer scrutiny of rare and specialty drug pricing continues.

Cardiometabolic RNAi programs could expand the market beyond rare disease.

Live Key Statistics

Pulled live from BriMindInvest's market-data pipeline at page load — the same feed that powers /analysis/ALNY. Fields the pipeline doesn't return this load are omitted rather than shown blank.

Current Price
$244.32
Market Cap
$32.69B
Trailing P/E
42.49
Forward P/E
19.59
52-Week High
$495.55
52-Week Low
$197.81
Beta
0.30
Revenue Growth (YoY)
+66.9%
Operating Margin
+17.9%
Return on Equity
+96.6%
Debt / Equity
220.62

Business Overview

Marketed RNAi therapeutics for rare genetic and other diseases.

A transthyretin franchise targeting nerve and heart disease.

Partnered products and royalties.

A pipeline in cardiometabolic, neurologic, and other diseases.

Segment Deep Dive

A closer look at each reporting segment individually, rather than treating the business as a single undifferentiated revenue line.

Transthyretin franchise

This is the most important growth driver, with treatments for polyneuropathy and cardiomyopathy. Share gains depend on differentiation and physician education.

Other rare disease products

Approved drugs for other rare conditions provide steady revenue. They are smaller but demonstrate the platform's breadth.

Pipeline and partnerships

Programs in hypertension and other conditions could widen the addressable population. Partnerships share development risk and provide royalties.

Capital Allocation & Balance Sheet Philosophy

How management has historically chosen to deploy cash — buybacks, dividends, R&D, and acquisitions — and what that reveals about capital discipline.

The company has funded itself through equity, partnerships, and royalty arrangements.

Profitability inflection reduces reliance on external capital.

R&D spending is significant and is directed toward platform expansion.

Convertible or structured financing has been used in the past.

Management & Governance

Leadership, incentive alignment, and governance structure — factors that shape execution risk independent of the underlying business model.

Scientific leadership and a long-term platform vision guide the company.

Management sets milestones for launches and profitability.

Governance is conventional for a biotech; review the proxy for details.

Execution on commercial scale-up is the main test.

See exactly how we get ALNY's fair-value range

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Table: Method, Relevance, Implied Value
MethodRelevanceImplied Value
Our DCF ModelHigh
Our P/E BasedMedium
Our Book Value BasedLow
Graham NumberLow
ROIC BasedLow
FCF Yield BasedHigh

Forecast Revenue and Free Cash Flow

5-Year Monte Carlo Simulation

Included with a subscription or a one-time purchase of this Alnylam Pharmaceuticals report:

  • Fair value from 7 methods, weighted by relevance to this business
  • 5-year financial forecast and DCF/earnings sensitivity grids
  • Decomposed AI Score, Monte Carlo simulation, and institutional/analyst data

$3.99 is less than one bad options trade — see the model before you commit real money. And it goes straight to the small team building this, not a hedge fund's marketing budget.

Bull Case vs. Bear Case

Bull Case
  • Cardiomyopathy uptake exceeds expectations.
  • Profitability expands quickly.
  • Pipeline programs succeed.
  • The platform yields additional approvals.
  • Partnerships provide royalty income.
Bear Case
  • Competitors take share.
  • Pricing or reimbursement is pressured.
  • Pipeline setbacks occur.
  • Launch execution disappoints.
  • High valuation compresses on slower growth.

Related Reports

In-depth reports for other names in Alnylam Pharmaceuticals's comparable set.

Vertex Pharmaceuticals
VRTX In-Depth Report
Regeneron Pharmaceuticals
REGN In-Depth Report
CRISPR Therapeutics
CRSP In-Depth Report
Moderna
MRNA In-Depth Report
Biogen
BIIB In-Depth Report
Amgen
AMGN In-Depth Report

4 catalysts and 4 risks we're tracking for ALNY

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Table: Catalyst, Expected Impact, Timeframe
CatalystExpected ImpactTimeframe

Included with a subscription or a one-time purchase of this Alnylam Pharmaceuticals report:

  • Catalyst list, each tagged with expected impact and timing
  • Risk register scored by probability and severity
  • 4 key metrics to watch before the next earnings report

$3.99 is less than one bad options trade — see the model before you commit real money. And it goes straight to the small team building this, not a hedge fund's marketing budget.

What Would Change Our Mind?

Specific, falsifiable triggers — not vague sentiment — that would move us toward or away from the bull case above.

Would Turn Us More Bullish
  • Cardiomyopathy uptake keeps accelerating
  • Operating margins rise quickly
  • Pipeline data broaden the market
Would Turn Us More Cautious
  • Competitors win a large share
  • Growth slows abruptly
  • Late-stage trials fail

Competitive Positioning

Alnylam's moat is RNAi intellectual property, delivery technology, and manufacturing know-how.

Ionis, Pfizer, BridgeBio, and others compete in transthyretin disease.

Physician familiarity and clinical outcomes drive prescribing.

The vulnerability is competition and reliance on a limited number of products.

Investor Decision Framework

A process for using this report, not a recommendation — how to weigh valuation, scenario spread, and your own risk tolerance.

  • Own it if you want a platform biotech with commercial traction.
  • Skip it if you cannot tolerate volatility or valuation risk.
  • Track product revenue and patient uptake.

The BriMindInvest Edge

Why this report is different from asking a general-purpose AI chatbot about the stock.

  • Every valuation number on this page is computed live from current market data through our own DCF, scoring, and Monte Carlo engines — not summarized or paraphrased from other analysts' reports the way a general chatbot would.
  • The relevance-weighted fair value, reverse-DCF market-implied growth, fundamentals-based Monte Carlo, and scenario tables above are proprietary calculations you cannot get by asking a general-purpose AI for "ALNY fair value" — those answers come from web summaries of other people's price targets, not a live, disclosed-assumption model.
  • Our 1-year price-target model has a real, published backtest (see Model Track Record above where covered) — we show our work and our error rate rather than asserting accuracy.
  • Numbers here are refreshed every time you load the page, not cached from a training cutoff months or years in the past.

Data Sources & Methodology

Valuation, price, and financial-statistics data in this report are fetched live from our production market-data pipeline (Yahoo Finance and Finnhub) at the time you loaded this page. The AI Score is a percentile ranking against our full covered stock universe, recomputed nightly. The fundamentals-based Monte Carlo and Bull/Base/Bear scenarios randomize growth rate, discount rate, and terminal growth around the same disclosed DCF assumptions used in the valuation table — they are not derived from resampled historical stock returns. The secondary historical-volatility simulation (2,000 bootstrap paths, seeded for reproducibility) uses the stock's own historical monthly returns and is shown separately because it measures a different thing (volatility) than the fundamentals-based model (intrinsic value).

This report is for informational and educational purposes only and does not constitute financial, investment, or tax advice, or a recommendation to buy or sell any security. All valuation models, price targets, and simulations are estimates based on historical and current data; actual results will differ, potentially substantially. Investing involves risk, including loss of principal. See our full Methodology and Disclaimer.

Free vs. Premium: What You're Getting

Free Article
  • Narrative overview and general bull/bear framing
  • Headline price and basic company facts
  • No live valuation model, AI Score, or forecast table
This Premium Report
  • Relevance-weighted fair value range and reverse-DCF market-implied growth
  • 5-year financial forecast, DCF sensitivity grid, and Bull/Base/Bear scenario table
  • Fundamentals-based Monte Carlo and decomposed AI Score with sub-factor components
  • Real, published backtested accuracy where ALNY is in our coverage set

Glossary of Key Terms

Plain-English definitions for the terms used throughout this report, for readers newer to equity valuation.

RNAi
RNA interference, a natural process used to silence specific genes.
Transthyretin amyloidosis
A disease where misfolded protein builds up in the heart and nerves.
Royalty
A payment based on partners' sales of a licensed product.

Frequently Asked Questions

What is RNAi?
A method that reduces production of disease-causing proteins by silencing genes.
What is Alnylam's biggest product opportunity?
Treatment of transthyretin amyloidosis, especially the cardiac form.
Is Alnylam profitable?
It has been moving toward profitability as sales grow.
What is the main risk?
Competition and pipeline setbacks.
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Data sources & disclosures: Financial data and metrics cited in this article are sourced from company SEC filings, earnings releases, and investor relations materials. Market prices and fundamental data are provided by financial market data providers. Market size estimates and industry projections are sourced from industry research and analyst reports. Figures reflect information available at the time of writing and may have changed. AI scores and price targets are proprietary estimates — see our Methodology. This article is for informational and educational purposes only and does not constitute financial advice or a recommendation to buy or sell any security. Investing involves risk, including the possible loss of principal. Please read our full Disclaimer and consult a licensed financial adviser before making investment decisions.